A Amalfitano, A R Bengur, R P Morse, J M Majure, L E Case, D L Veerling, J Mackey, P Kishnani, W Smith, A McVie-Wylie, J A Sullivan, G E Hoganson, J A Phillips, G B Schaefer, J Charrow, R E Ware, E H Bossen, and Y T Chen (2001)

Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: results of a phase I/II clinical trial

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